Retroviral vector design studies toward hematopoietic stem cell gene therapy for mucopolysaccharidosis type I
Author:
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.nature.com/articles/3301298.pdf
Reference55 articles.
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4. Rettinger SD et al. Liver-directed gene therapy: quantitative evaluation of promoter elements by using in vivo retroviral transduction Proc Natl Acad Sci USA 1994 91: 1460–1464
5. Scharfmann R, Axelrod JH, Verma IM . Long-term in vivo expression of retrovirus-mediated gene transfer in mouse fibroblast implants Proc Natl Acad Sci USA 1991 88: 4626–4630
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