Successful therapeutic effect in a mouse model of erythropoietic protoporphyria by partial genetic correction and fluorescence-based selection of hematopoietic cells-Reference-Cited by-同舟云学术

Successful therapeutic effect in a mouse model of erythropoietic protoporphyria by partial genetic correction and fluorescence-based selection of hematopoietic cells

Published:2001-04 Issue:8 Volume:8 Page:618-626
ISSN:0969-7128
Container-title:Gene Therapy
language:en
Short-container-title:Gene Ther

Author:

Fontanellas A,Mendez M,Mazurier F,Cario-André M,Navarro S,Ged C,Taine L,Géronimi F,Richard E,Moreau-Gaudry F,Enriquez de Salamanca R,de Verneuil H

Publisher

Springer Science and Business Media LLC

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.nature.com/articles/3301427.pdf

Reference36 articles.

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2. Todd DJ . Erythropoietic protoporphyria Br J Dermatol 1994 131: 751–766

3. Baart de la Faille H et al. Erythropoietic protoporphyria: clinical aspect with emphasis on the skin Curr Probl Dermatol 1991 20: 123–135

4. Bloomer JR . The liver in protoporphyria Hepatology 1988 8: 402–407

5. Doss MO, Frank M . Hepatobiliary implications and complications in protoporphyria, a 20 year study Clin Biochem 1989 22: 223–229

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