CRISPR/Cas9-mediated genome editing via postnatal administration of AAV vector cures haemophilia B mice-Reference-Cited by-同舟云学术

CRISPR/Cas9-mediated genome editing via postnatal administration of AAV vector cures haemophilia B mice

Published:2017-06-23 Issue:1 Volume:7 Page:
ISSN:2045-2322
Container-title:Scientific Reports
language:en
Short-container-title:Sci Rep

Author:

Ohmori Tsukasa,Nagao Yasumitsu,Mizukami Hiroaki,Sakata Asuka,Muramatsu Shin-ichi^ORCID,Ozawa Keiya,Tominaga Shin-ichi,Hanazono Yutaka,Nishimura Satoshi,Nureki Osamu,Sakata Yoichi

Publisher

Springer Science and Business Media LLC

Subject

Multidisciplinary

Link

http://www.nature.com/articles/s41598-017-04625-5.pdf

Reference39 articles.

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2. Manco-Johnson, M. J. et al. Prophylaxis versus episodic treatment to prevent joint disease in boys with severe hemophilia. The New England journal of medicine 357, 535–544, doi: 10.1056/NEJMoa067659 (2007).

3. Hsu, P. D., Lander, E. S. & Zhang, F. Development and applications of CRISPR-Cas9 for genome engineering. Cell 157, 1262–1278, doi: 10.1016/j.cell.2014.05.010 (2014).

4. Jiang, W. & Marraffini, L. A. CRISPR-Cas: New Tools for Genetic Manipulations from Bacterial Immunity Systems. Annu Rev Microbiol 69, 209–228, doi: 10.1146/annurev-micro-091014-104441 (2015).

5. Doudna, J. A. & Charpentier, E. Genome editing. The new frontier of genome engineering with CRISPR-Cas9. Science 346, 1258096, doi: 10.1126/science.1258096 (2014).

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