Towards personalised allele-specific CRISPR gene editing to treat autosomal dominant disorders-Reference-Cited by-同舟云学术

Towards personalised allele-specific CRISPR gene editing to treat autosomal dominant disorders

Published:2017-11-23 Issue:1 Volume:7 Page:
ISSN:2045-2322
Container-title:Scientific Reports
language:en
Short-container-title:Sci Rep

Author:

Christie Kathleen A.,Courtney David G.,DeDionisio Larry A.^ORCID,Shern Connie Chao^ORCID,De Majumdar Shyamasree,Mairs Laura C.,Nesbit M. Andrew,Moore C. B. Tara

Publisher

Springer Science and Business Media LLC

Subject

Multidisciplinary

Link

http://www.nature.com/articles/s41598-017-16279-4.pdf

Reference43 articles.

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2. Mali, P. et al. RNA-guided human genome engineering via Cas9. Science. 339(6121), 823–6 (2013)

3. Cong, L. et al. Multiplex genome engineering using CRISPR/Cas systems. Science. 339(6121), 819–23 (2013).

4. Ran, F. A. et al. Genome engineering using the CRISPR-Cas9 system. Nat Protoc. 8(11), 2281–308 (2013).

5. Yin, H. et al. Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo. Nat Biotechnol. 34(3), 328–33 (2016).

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