Large animal models and gene therapy
Author:
Publisher
Springer Science and Business Media LLC
Subject
Genetics (clinical),Genetics
Link
http://www.nature.com/articles/5201535.pdf
Reference83 articles.
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4. Ohshima T, Murray GJ, Swaim WD et al: Alpha-galactosidase A deficient mice: a model of Fabry disease. Proc Natl Acad Sci USA 1997; 94: 2540–2544.
5. Phaneuf D, Wakamatsu N, Huang JQ et al: Dramatically different phenotypes in mouse models of human Tay-Sachs and Sandhoff diseases. Hum Mol Genet 1996; 5: 1–14.
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