Nusinersen potentially effective in SMA
Author:
Publisher
Springer Science and Business Media LLC
Subject
Cellular and Molecular Neuroscience,Neurology (clinical)
Link
http://www.nature.com/articles/nrneurol.2016.199.pdf
Reference1 articles.
1. Finkel, R. S. et al. Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study. Lancet http://dx.doi.org/10.1016/S0140-6736(16)31408-8 (2016)
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