1. Chang, A.G.Y. & Wu, G.Y. Gene therapy: Applications to the treatment of gastrointestinal and liver diseases. Gastroenterology 106, 1076–1084 (1994).
2. Teckman, J.H., Qu, D. & Perlmutter, D.H. Molecular pathogenesis of liver disease in α1-antitrypsin deficiency. Hepatology 24, 1504–1516 (1996).
3. Reiner, A.P. & Davie, E.W., Metabolic and Molecular Bases of Inherited Disease. (eds. Scriver, C.R., Beaudet, A.L., Sly, W.S. & Valle, D.) 3181–3221 (McGraw-Hill, Inc., New York, 1995).
4. Strauss, M. Liver-directed gene therapy: Prospects and problems. Gene Ther 1, 156–164 (1994).
5. Bowles, N., Woo, S.L.C. Gene therapy for metabolic disorders. Advanced Drug Del. Rev. 17, 293–302 (1995).