A novel, long-lived, and highly engraftable immunodeficient mouse model of mucopolysaccharidosis type I-Reference-Cited by-同舟云学术

A novel, long-lived, and highly engraftable immunodeficient mouse model of mucopolysaccharidosis type I

Published:2015 Issue: Volume:2 Page:14068
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Mendez Daniel C,Stover Alexander E,Rangel Anthony D,Brick David J,Nethercott Hubert E,Torres Marissa A,Khalid Omar,Wong Andrew MS,Cooper Jonathan D,Jester James V,Monuki Edwin S,McGuire Cian,Le Steven Q,Kan Shih-hsin,Dickson Patricia I,Schwartz Philip H

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference42 articles.

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5. Laronidase treatment of mucopolysaccharidosis I;Wraith;BioDrugs,2005

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