Persistent Expression of FLAG-tagged Micro dystrophin in Nonhuman Primates Following Intramuscular and Vascular Delivery-Reference-Cited by-同舟云学术

Persistent Expression of FLAG-tagged Micro dystrophin in Nonhuman Primates Following Intramuscular and Vascular Delivery

Published:2010-01 Issue:1 Volume:18 Page:109-117
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Rodino-Klapac Louise R,Montgomery Chrystal L,Bremer William G,Shontz Kimberly M,Malik Vinod,Davis Nancy,Sprinkle Spencer,Campbell Katherine J,Sahenk Zarife,Clark K Reed,Walker Christopher M,Mendell Jerry R,Chicoine Louis G

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference27 articles.

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3. Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy;Harper;Nat Med,2002

4. Adeno-associated virus-mediated microdystrophin expression protects young mdx muscle from contraction-induced injury;Liu;Mol Ther,2005

5. A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy;Rodino-Klapac;J Transl Med,2007

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