Rescue of Pyruvate Kinase Deficiency in Mice by Gene Therapy Using the Human Isoenzyme-Reference-Cited by-同舟云学术

Rescue of Pyruvate Kinase Deficiency in Mice by Gene Therapy Using the Human Isoenzyme

Published:2009-12 Issue:12 Volume:17 Page:2000-2009
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Meza Nestor W,Alonso-Ferrero Maria E,Navarro Susana,Quintana-Bustamante Oscar,Valeri Antonio,Garcia-Gomez Maria,Bueren Juan A,Bautista Jose M,Segovia Jose C

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference46 articles.

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3. Concise review: pyruvate kinase deficiency: historical perspective and recent progress of molecular genetics;Miwa;Am J Hematol,1993

4. Molecular basis of impaired pyruvate kinase isozyme conversion in erythroid cells: a single amino acid substitution near the active site and decreased mRNA content of the R-type PK;Kanno;Biochem Biophys Res Commun,1993

5. Red cell enzymopathies of the glycolytic pathway;Tanaka;Semin Hematol,1990

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