Short-term Correction of Arginase Deficiency in a Neonatal Murine Model With a Helper-dependent Adenoviral Vector-Reference-Cited by-同舟云学术

Short-term Correction of Arginase Deficiency in a Neonatal Murine Model With a Helper-dependent Adenoviral Vector

Published:2009-07 Issue:7 Volume:17 Page:1155-1163
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Gau Chia-Ling,Rosenblatt Robin A,Cerullo Vincenzo,Lay Fides D,Dow Adrienne C,Livesay Justin,Brunetti-Pierri Nicola,Lee Brendan,Cederbaum Stephen D,Grody Wayne W,Lipshutz Gerald S

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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5. Efficient, long-term hepatic gene transfer using clinically relevant HDAd doses by balloon occlusion catheter delivery in nonhuman primates;Brunetti-Pierri;Mol Ther,2009

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