Cationic PMMA Nanoparticles Bind and Deliver Antisense Oligoribonucleotides Allowing Restoration of Dystrophin Expression in the mdx Mouse-Reference-Cited by-同舟云学术

Cationic PMMA Nanoparticles Bind and Deliver Antisense Oligoribonucleotides Allowing Restoration of Dystrophin Expression in the mdx Mouse

Published:2009-05 Issue:5 Volume:17 Page:820-827
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Rimessi Paola,Sabatelli Patrizia,Fabris Marina,Braghetta Paola,Bassi Elena,Spitali Pietro,Vattemi Gaetano,Tomelleri Giuliano,Mari Lara,Perrone Daniela,Medici Alessandro,Neri Marcella,Bovolenta Matteo,Martoni Elena,Maraldi Nadir M.,Gualandi Francesca,Merlini Luciano,Ballestri Marco,Tondelli Luisa,Sparnacci Katia,Bonaldo Paolo,Caputo Antonella,Laus Michele,Ferlini Alessandra

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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