Evidence for Long-term Efficacy and Safety of Gene Therapy for Wiskott–Aldrich Syndrome in Preclinical Models-Reference-Cited by-同舟云学术

Evidence for Long-term Efficacy and Safety of Gene Therapy for Wiskott–Aldrich Syndrome in Preclinical Models

Published:2009-06 Issue:6 Volume:17 Page:1073-1082
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Marangoni Francesco,Bosticardo Marita,Charrier Sabine,Draghici Elena,Locci Michela,Scaramuzza Samantha,Panaroni Cristina,Ponzoni Maurilio,Sanvito Francesca,Doglioni Claudio,Liabeuf Marie,Gjata Bernard,Montus Marie,Siminovitch Katherine,Aiuti Alessandro,Naldini Luigi,Dupré Loïc,Roncarolo Maria Grazia,Galy Anne,Villa Anna

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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4. Studies of the expression of the Wiskott-Aldrich syndrome protein;Stewart;J Clin Invest,1996

5. Autoinhibition and activation mechanisms of the Wiskott-Aldrich syndrome protein;Kim;Nature,2000

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