The Pleiotropic Effects of Natural AAV Infections on Liver-directed Gene Transfer in Macaques-Reference-Cited by-同舟云学术

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The Pleiotropic Effects of Natural AAV Infections on Liver-directed Gene Transfer in Macaques

Published:2010-01 Issue:1 Volume:18 Page:126-134
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Wang Lili,Calcedo Roberto,Wang Huan,Bell Peter,Grant Rebecca,Vandenberghe Luk H,Sanmiguel Julio,Morizono Hiroki,Batshaw Mark L,Wilson James M

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference40 articles.

1. Safety and efficacy of gene transfer for Leber's congenital amaurosis;Maguire;N Engl J Med,2008

2. Effect of gene therapy on visual function in Leber's congenital amaurosis;Bainbridge;N Engl J Med,2008

3. Treatment of Leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial;Hauswirth;Hum Gene Ther,2008

4. Safety and tolerability of gene therapy with an adeno-associated virus (AAV) borne GAD gene for Parkinson's disease: an open label, phase I trial;Kaplitt;Lancet,2007

5. Results from a phase I safety trial of hAADC gene therapy for Parkinson disease;Eberling;Neurology,2008

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4. Prevalence of Adeno-Associated Virus-9-Neutralizing Antibody in Chinese Patients with Duchenne Muscular Dystrophy;Human Gene Therapy;2024-01-01

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