Systemic Correction of Storage Disease in MPS I NOD/SCID Mice Using the Sleeping Beauty Transposon System

Author:

Aronovich Elena L,Bell Jason B,Khan Shaukat A,Belur Lalitha R,Gunther Roland,Koniar Brenda,Schachern Patricia A,Parker Josh B,Carlson Cathy S,Whitley Chester B,McIvor R Scott,Gupta Pankaj,Hackett Perry B

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference50 articles.

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3. Cell and gene-based therapies for the lysosomal storage diseases;Hodges;Curr Gene Ther,2006

4. Limitations of enzyme replacement therapy: current and future;Wraith;J Inherit Metab Dis,2006

5. Gene therapy for mucopolysaccharidosis;Ponder;Expert Opin Biol Ther,2007

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