Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector-Reference-Cited by-同舟云学术

Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector

Published:2000-03 Issue:3 Volume:24 Page:257-261
ISSN:1061-4036
Container-title:Nature Genetics
language:en
Short-container-title:Nat Genet

Author:

Kay Mark A.,Manno Catherine S.,Ragni Margaret V.,Larson Peter J.,Couto Linda B.,McClelland Alan,Glader Bertil,Chew Amy J.,J Tai Shing,Herzog Roland W.,Arruda Valder,Johnson Fred,Scallan Ciaran,Skarsgard Erik,Flake Alan W.,High Katherine A.

Publisher

Springer Science and Business Media LLC

Subject

Genetics

Link

http://www.nature.com/articles/ng0300_257.pdf

Reference16 articles.

1. Herzog, R.W. et al. Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus . Proc. Natl Acad. Sci. USA 94, 5804– 5809 (1997).

2. Herzog, R. et al. Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector. Nature Med. 5, 56–63 ( 1999).

3. Ljung, R.C.R. Annotation. Can haemophilic arthropathy be prevented? Br. J. Haematol. 101, 215–219 ( 1998).

4. Lofqvist, T., Nilsson, I.M., Berntorp, E. & Pettersson, H. Haemophilia prophylaxis in young patients—a long term follow up. J. Intern. Med. 241, 395–400 (1997).

5. Mannucci, P.M. & Weitz, J.I. The hemophilias: progress and problems . Semin. Hematol. 36, 104– 117 (1999).

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