Non-immunogenic utrophin gene therapy for the treatment of muscular dystrophy animal models-Reference-Cited by-同舟云学术

Non-immunogenic utrophin gene therapy for the treatment of muscular dystrophy animal models

Published:2019-10 Issue:10 Volume:25 Page:1505-1511
ISSN:1078-8956
Container-title:Nature Medicine
language:en
Short-container-title:Nat Med

Author:

Song Yafeng,Morales Leon^ORCID,Malik Alock S.,Mead Andrew F.,Greer Christopher D.^ORCID,Mitchell Marilyn A.,Petrov Mihail T.,Su Leonard T.,Choi Margaret E.,Rosenblum Shira T.,Lu Xiangping,VanBelzen Daniel J.^ORCID,Krishnankutty Ranjith K.,Balzer Frederick J.,Loro Emanuele,French Robert^ORCID,Propert Kathleen J.,Zhou Shangzhen,Kozyak Benjamin W.,Nghiem Peter P.,Khurana Tejvir S.,Kornegay Joe N.,Stedman Hansell H.^ORCID

Publisher

Springer Science and Business Media LLC

Subject

General Biochemistry, Genetics and Molecular Biology,General Medicine

Link

http://www.nature.com/articles/s41591-019-0594-0.pdf

Reference53 articles.

1. Hoffman, E. P., Brown, R. H. Jr. & Kunkel, L. M. Dystrophin: the protein product of the Duchenne muscular dystrophy locus. Cell 51, 919–928 (1987).

2. Koenig, M., Monaco, A. P. & Kunkel, L. M. The complete sequence of dystrophin predicts a rod-shaped cytoskeletal protein. Cell 53, 219–226 (1988).

3. Petrof, B. J., Shrager, J. B., Stedman, H. H., Kelly, A. M. & Sweeney, H. L. Dystrophin protects the sarcolemma from stresses developed during muscle contraction. Proc. Natl Acad. Sci. USA 90, 3710–3714 (1993).

4. Ibraghimov-Beskrovnaya, O. et al. Primary structure of dystrophin-associated glycoproteins linking dystrophin to the extracellular matrix. Nature 355, 696–702 (1992).

5. Tinsley, J. M. et al. Primary structure of dystrophin-related protein. Nature 360, 591–593 (1992).

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