Improved gene delivery to adult mouse spinal cord through the use of engineered hybrid adeno-associated viral serotypes
Author:
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
https://www.nature.com/articles/gt201727.pdf
Reference23 articles.
1. Kotterman MA, Schaffer DV . Engineering adeno-associated viruses for clinical gene therapy. Nat Rev Genet 2014; 15: 445–451.
2. Mingozzi F, High KA . Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges. Nat Rev Genet 2011; 12: 341–355.
3. Asokan A, Schaffer DV, Samulski RJ . The AAV vector toolkit: poised at the clinical crossroads. Mol Ther 2012; 20: 699–708.
4. Charbel Issa P, De Silva SR, Lipinski DM, Singh MS, Mouravlev A, You Q et al. Assessment of tropism and effectiveness of new primate-derived hybrid recombinant AAV serotypes in the mouse and primate retina. PLoS ONE 2013; 8: e60361.
5. Mizukami H, Mimuro J, Ogura T, Okada T, Urabe M, Kume A et al. Adipose tissue as a novel target for in vivo gene transfer by adeno-associated viral vectors. Hum Gene Ther 2006; 17: 921–928.
Cited by 14 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. Adeno-Associated Virus Engineering and Load Strategy for Tropism Modification, Immune Evasion and Enhanced Transgene Expression;International Journal of Nanomedicine;2024-07
2. AAV Engineering for Improving Tropism to the Central Nervous System;Biology;2023-01-26
3. AAV vectors: The Rubik’s cube of human gene therapy;Molecular Therapy;2022-12
4. Viral strategies for targeting spinal neuronal subtypes in adult wild-type rodents;Scientific Reports;2022-05-23
5. Adeno-Associated Virus Vector for Central Nervous System Gene Therapy;Trends in Molecular Medicine;2021-06
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3