Author:
Hickey D G,Edwards T L,Barnard A R,Singh M S,de Silva S R,McClements M E,Flannery J G,Hankins M W,MacLaren R E
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,Molecular Medicine
Reference47 articles.
1. Liew G, Michaelides M, Bunce C . A comparison of the causes of blindness certifications in England and Wales in working age adults (16-64 years), 1999-2000 with 2009-2010. Br Med J 2014; 4: e004015.
2. Edwards TL, Jolly JK, Groppe M, Barnard AR, Cottriall CL, Tolmachova T et al. Visual acuity after retinal gene therapy for choroideremia. N Engl J Med 2016; 374: 1996–1998.
3. Jacobson SG, Cideciyan AV, Ratnakaram R, Heon E, Schwartz SB, Roman AJ et al. Gene therapy for leber congenital amaurosis caused by RPE65 Mutations: safety and efficacy in 15 children and adults followed up to 3 years. Arch Ophthalmol 2012; 130: 9–24.
4. Wu Y, Liang D, Wang Y, Bai M, Tang W, Bao S et al. Correction of a genetic disease in mouse via use of CRISPR-Cas9. Cell Stem Cell 2013; 13: 659–662.
5. Millington-Ward S, Chadderton N, O’Reilly M, Palfi A, Goldmann T, Kilty C et al. Suppression and replacement gene therapy for autosomal dominant disease in a murine model of dominant retinitis pigmentosa. Mol Ther 2011; 19: 642–649.
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