Long-Term Correction of Sandhoff Disease Following Intravenous Delivery of rAAV9 to Mouse Neonates-Reference-Cited by-同舟云学术

Long-Term Correction of Sandhoff Disease Following Intravenous Delivery of rAAV9 to Mouse Neonates

Published:2015-03 Issue:3 Volume:23 Page:414-422
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Walia Jagdeep S,Altaleb Naderah,Bello Alexander,Kruck Christa,LaFave Matthew C,Varshney Gaurav K,Burgess Shawn M,Chowdhury Biswajit,Hurlbut David,Hemming Richard,Kobinger Gary P,Triggs-Raine Barbara

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference50 articles.

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3. Some Epidemiologic and Genetic Aspects of Tay Sachs Disease;Myrianthopoulos,1962

4. Genetic variants of Tay-Sachs disease: Tay-Sachs disease and Sandhoff's disease in French Canadians, juvenile Tay-Sachs disease in Lebanese Canadians, and a Tay-Sachs screening program in the French-Canadian population;Andermann;Prog Clin Biol Res,1977

5. Carrier detection in Sandhoff disease;Lowden;Am J Hum Genet,1978

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