Corrective GUSB Transfer to the Canine Mucopolysaccharidosis VII Brain-Reference-Cited by-同舟云学术

Corrective GUSB Transfer to the Canine Mucopolysaccharidosis VII Brain

Published:2014-04 Issue:4 Volume:22 Page:762-773
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Cubizolle Aurelie,Serratrice Nicolas,Skander Nadia,Colle Marie-Anne,Ibanes Sandy,Gennetier Aurelie,Bayo-Puxan Neus,Mazouni Khalil,Mennechet Franck,Joussemet Beatrice,Cherel Yan,Lajat Yaouen,Vite Charles,Bernex Florence,Kalatzis Vasiliki,Haskins Mark E,Kremer Eric J

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference52 articles.

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4. From serendipity to therapy;Neufeld;Annu Rev Biochem,2011

5. Gene transfer to the central nervous system: current state of the art of the viral vectors;Kremer;Curr Genomics,2005

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