Manipulation of mtDNA heteroplasmy in all striated muscles of newborn mice by AAV9-mediated delivery of a mitochondria-targeted restriction endonuclease-Reference-Cited by-同舟云学术

Manipulation of mtDNA heteroplasmy in all striated muscles of newborn mice by AAV9-mediated delivery of a mitochondria-targeted restriction endonuclease

Published:2011-12-01 Issue:11 Volume:19 Page:1101-1106
ISSN:0969-7128
Container-title:Gene Therapy
language:en
Short-container-title:Gene Ther

Author:

Bacman S R,Williams S L,Duan D,Moraes C T

Publisher

Springer Science and Business Media LLC

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.nature.com/articles/gt2011196.pdf

Reference37 articles.

1. Kyriakouli DS, Boesch P, Taylor RW, Lightowlers RN . Progress and prospects: gene therapy for mitochondrial DNA disease. Gene Therapy 2008; 15: 1017–1023.

2. Cwerman-Thibault H, Sahel JA, Corral-Debrinski M . Mitochondrial medicine: to a new era of gene therapy for mitochondrial DNA mutations. J Inherit Metab Dis 2011; 34: 327–344.

3. Thorburn DR, Dahl HH . Mitochondrial disorders: genetics, counseling, prenatal diagnosis and reproductive options. Am J Med Genet 2001; 106: 102–114.

4. DiMauro S, Schon EA . Mitochondrial respiratory-chain diseases. N Engl J Med 2003; 348: 2656–2668.

5. Srivastava S, Moraes CT . Manipulating mitochondrial DNA heteroplasmy by a mitochondrially targeted restriction endonuclease. Hum Mol Genet 2001; 10: 3093–3099.

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