Guidelines for Antisense Oligonucleotide Design and Insight Into Splice-modulating Mechanisms-Reference-Cited by-同舟云学术

Guidelines for Antisense Oligonucleotide Design and Insight Into Splice-modulating Mechanisms

Published:2009-03 Issue:3 Volume:17 Page:548-553
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Aartsma-Rus Annemieke,van Vliet Laura,Hirschi Marscha,Janson Anneke AM,Heemskerk Hans,de Winter Christa L,de Kimpe Sjef,van Deutekom Judith CT,'t Hoen Peter AC,van Ommen Gert-Jan B

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference23 articles.

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2. RNA modulation, repair and remodeling by splice switching oligonucleotides;Kole;Acta Biochim Pol,2004

3. Effective targeted gene “knockdown” in zebrafish;Nasevicius;Nat Genet,2000

4. Local dystrophin restoration with antisense oligonucleotide PRO051;van Deutekom;N Engl J Med,2007

5. Mfold web server for nucleic acid folding and hybridization prediction;Zuker;Nucleic Acids Res,2003

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