AAV Vector-mediated Reversal of Hypoglycemia in Canine and Murine Glycogen Storage Disease Type Ia-Reference-Cited by-同舟云学术

AAV Vector-mediated Reversal of Hypoglycemia in Canine and Murine Glycogen Storage Disease Type Ia

Published:2008-04 Issue:4 Volume:16 Page:665-672
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Koeberl Dwight D,Pinto Carlos,Sun Baodong,Li Songtao,Kozink Daniel M,Benjamin Daniel K,Demaster Amanda K,Kruse Meghan A,Vaughn Valerie,Hillman Steven,Bird Andrew,Jackson Mark,Brown Talmage,Kishnani Priya S,Chen Yuan-Tsong

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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5. Early, sustained efficacy of adeno-associated virus vector-mediated gene therapy in glycogen storage disease type Ia;Koeberl;Gene Ther,2006

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