Base editing-mediated splicing correction therapy for spinal muscular atrophy
Author:
Publisher
Springer Science and Business Media LLC
Subject
Cell Biology,Molecular Biology
Link
http://www.nature.com/articles/s41422-020-0304-y.pdf
Reference11 articles.
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3. Cox, D. B., Platt, R. J. & Zhang, F. Nat. Med. 21, 121–131 (2015).
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5. Ran, F. A. et al. Nat. Protoc. 8, 2281–2308 (2013).
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