1. Brennan, T.A. & Wilson, J.M. Nat. Biotechnol. 32, 874–876 (2014).
2. Ylä-Herttuala, S. Mol. Ther. 23, 217–218 (2015).
3. Hirschler, B. GSK readies “bubble boy” drug as big pharma bets on gene therapy. Reuters (27 April 2015).
http://www.reuters.com/article/2015/04/27/healthgenetherapy-gsk-idUSL5N0XK2K120150427
4. Leleu, H. et al. J. Viral Hepat. 22, 376–383 (2015).
5. Hanson, S.G. & Bentley, T.S. 2014 US organ and tissue transplant cost estimates and discussions (Milliman Research, 30 December 2014).