Intrathecal delivery of frataxin mRNA encapsulated in lipid nanoparticles to dorsal root ganglia as a potential therapeutic for Friedreich’s ataxia-Reference-Cited by-同舟云学术

Intrathecal delivery of frataxin mRNA encapsulated in lipid nanoparticles to dorsal root ganglia as a potential therapeutic for Friedreich’s ataxia

Published:2016-02-17 Issue:1 Volume:6 Page:
ISSN:2045-2322
Container-title:Scientific Reports
language:en
Short-container-title:Sci Rep

Author:

Nabhan Joseph F.,Wood Kristy M.,Rao Varada P.,Morin Jeffrey,Bhamidipaty Surya,LaBranche Timothy P.,Gooch Renea L.,Bozal Fazli,Bulawa Christine E.,Guild Braydon C.

Publisher

Springer Science and Business Media LLC

Subject

Multidisciplinary

Link

http://www.nature.com/articles/srep20019.pdf

Reference41 articles.

1. Campuzano, V. et al. Friedreich’s ataxia: autosomal recessive disease caused by an intronic GAA triplet repeat expansion. Science 271, 1423–1427 (1996).

2. Morral, J. A., Davis, A. N., Qian, J., Gelman, B. B. & Koeppen, A. H. Pathology and pathogenesis of sensory neuropathy in Friedreich’s ataxia. Acta Neuropathol. 120, 97–108, 10.1007/s00401-010-0675-0 (2010).

3. Payne, R. M. & Wagner, G. R. Cardiomyopathy in Friedreich ataxia: clinical findings and research. J. Child Neurol. 27, 1179–1186, 10.1177/0883073812448535 (2012).

4. Weidemann, F. et al. Cardiomyopathy of friedreich ataxia. J. Neurochem. 126 Suppl, 88–93, 10.1111/jnc.12217 (2013).

5. Kumari, D., Biacsi, R. E. & Usdin, K. Repeat expansion affects both transcription initiation and elongation in friedreich ataxia cells. J. Biol. Chem. 286, 4209–4215, 10.1074/jbc.M110.194035 (2011).

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