Optimizing lentiviral vector transduction of hematopoietic stem cells for gene therapy-Reference-Cited by-同舟云学术

Optimizing lentiviral vector transduction of hematopoietic stem cells for gene therapy

Published:2020-04-27 Issue:12 Volume:27 Page:545-556
ISSN:0969-7128
Container-title:Gene Therapy
language:en
Short-container-title:Gene Ther

Author:

Jang Yoonjeong,Kim Yoon-Sang,Wielgosz Matthew M.,Ferrara Francesca^ORCID,Ma Zhijun,Condori Jose,Palmer Lance E.,Zhao Xiwen^ORCID,Kang Guolian,Rawlings David J.,Zhou Sheng,Ryu Byoung Y.

Funder

Assisi Foundation of Memphis

St. Jude Children's Research Hospital Research Consortium "Novel Gene Therapies for Sickle Cell Disease"

U.S. Department of Health & Human Services | NIH | National Heart, Lung, and Blood Institute

Publisher

Springer Science and Business Media LLC

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.nature.com/articles/s41434-020-0150-z.pdf

Reference40 articles.

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2. Kuo CY, Kohn DB. Gene therapy for the treatment of primary immune deficiencies. Curr Allergy Asthma Rep. 2016;16:39.

3. Cavazzana M, Bushman FD, Miccio A, André-Schmutz I, Six E. Gene therapy targeting haematopoietic stem cells for inherited diseases: progress and challenges. Nat Rev Drug Discov. 2019;18:447–62.

4. Thompson AA, Walters MC, Kwiatkowski J, Rasko JE, Ribeil J-A, Hongeng S, et al. Gene therapy in patients with transfusion-dependent β-thalassemia. New Eng J Med. 2018;378:1479–93.

5. Millington M, Arndt A, Boyd M, Applegate T, Shen S. Towards a clinically relevant lentiviral transduction protocol for primary human CD34+ hematopoietic stem/progenitor cells. PLoS ONE. 2009;4:e6461.

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