Pharmacological Chaperones as Therapeutics for Lysosomal Storage Diseases
Author:
Affiliation:
1. Amicus Therapeutics, 1 Cedar Brook Drive, Cranbury, New Jersey 08512, United States
2. Amicus Therapeutics, 11099 North Torrey Pines Road, La Jolla, California 92037, United States
Publisher
American Chemical Society (ACS)
Subject
Drug Discovery,Molecular Medicine
Link
https://pubs.acs.org/doi/pdf/10.1021/jm301557k
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