Central Nervous System Delivery and Biodistribution Analysis of an Antibody–Enzyme Fusion for the Treatment of Lafora Disease-Reference-Cited by-同舟云学术

Central Nervous System Delivery and Biodistribution Analysis of an Antibody–Enzyme Fusion for the Treatment of Lafora Disease

Published:2019-07-22 Issue:9 Volume:16 Page:3791-3801
ISSN:1543-8384
Container-title:Molecular Pharmaceutics
language:en
Short-container-title:Mol. Pharmaceutics

Author:

Austin Grant L.^ORCID,Simmons Zoe R.,Klier Jack E.,Rondon Alberto,Hodges Brad L.¹,Shaffer Robert¹,Aziz Nadine M.¹,McKnight Tracy R.¹,Pauly James R.²,Armstrong Dustin D.¹,Vander Kooi Craig W.,Gentry Matthew S.^ORCID

Affiliation:

1. Valerion Therapeutics, Concord, Massachusetts 01742, United States

2. Department of Pharmaceutical Sciences, University of Kentucky College of Pharmacy, Lexington, Kentucky 40536, United States

Funder

National Institute of Neurological Disorders and Stroke

Epilepsy Foundation

Valerion Therapeutics

Biospecimen Procurement and Translational Pathology Shared Resource Facility of the University of Kentucky Markey Cancer Center

Publisher

American Chemical Society (ACS)

Subject

Drug Discovery,Pharmaceutical Science,Molecular Medicine

Link

https://pubs.acs.org/doi/pdf/10.1021/acs.molpharmaceut.9b00396

Reference51 articles.

1. Lafora disease: insights into neurodegeneration from plant metabolism

2. Lafora disease offers a unique window into neuronal glycogen metabolism

3. Lafora disease

4. Idiopathic Epilepsies with a Complex Mode of Inheritance

5. Astrocytes: new players in progressive myoclonus epilepsy of Lafora type

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