Reduction in Brain Heparan Sulfate with Systemic Administration of an IgG Trojan Horse–Sulfamidase Fusion Protein in the Mucopolysaccharidosis Type IIIA Mouse-Reference-Cited by-同舟云学术

Reduction in Brain Heparan Sulfate with Systemic Administration of an IgG Trojan Horse–Sulfamidase Fusion Protein in the Mucopolysaccharidosis Type IIIA Mouse

Published:2017-12-29 Issue:2 Volume:15 Page:602-608
ISSN:1543-8384
Container-title:Molecular Pharmaceutics
language:en
Short-container-title:Mol. Pharmaceutics

Author:

Boado Ruben J.¹,Lu Jeff Zhiqiang¹,Hui Eric Ka-Wai¹,Pardridge William M.¹^ORCID

Affiliation:

1. ArmaGen, Inc., Calabasas, California 91302, United States

Publisher

American Chemical Society (ACS)

Subject

Drug Discovery,Pharmaceutical Science,Molecular Medicine

Link

https://pubs.acs.org/doi/pdf/10.1021/acs.molpharmaceut.7b00958

Reference31 articles.

1. Cloning of the sulphamidase gene and identification of mutations in Sanfilippo A syndrome

2. Mucopolysaccharidosis type IIIA: Clinical spectrum and genotype-phenotype correlations

3. A Multiplex Assay for the Diagnosis of Mucopolysaccharidoses and Mucolipidoses

4. Disease stage determines the efficacy of treatment of a paediatric neurodegenerative disease

5. CSF, blood-brain barrier, and brain drug delivery

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