Reversal of Lysosomal Storage in Brain of Adult MPS-I Mice with Intravenous Trojan Horse-Iduronidase Fusion Protein
Author:
Affiliation:
1. Department of Medicine, UCLA, Los Angeles, California 90024, United States
2. ArmaGen Technologies, Inc., Santa Monica, California 90401, United States
Publisher
American Chemical Society (ACS)
Subject
Drug Discovery,Pharmaceutical Science,Molecular Medicine
Link
https://pubs.acs.org/doi/pdf/10.1021/mp200136x
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5. Enzyme replacement therapy in mucopolysaccharidosis type I: Progress and emerging difficulties
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