An iPSC-Derived Neuron Model of CLN3 Disease Facilitates Small Molecule Phenotypic Screening-Reference-Cited by-同舟云学术

An iPSC-Derived Neuron Model of CLN3 Disease Facilitates Small Molecule Phenotypic Screening

Published:2020-09-01 Issue:5 Volume:3 Page:931-947
ISSN:2575-9108
Container-title:ACS Pharmacology & Translational Science
language:en
Short-container-title:ACS Pharmacol. Transl. Sci.

Author:

Kinarivala Nihar¹^ORCID,Morsy Ahmed²,Patel Ronak¹,Carmona Angelica V.²,Sajib Md. Sanaullah¹^ORCID,Raut Snehal¹,Mikelis Constantinos M.¹^ORCID,Al-Ahmad Abraham¹,Trippier Paul C.²¹³^ORCID

Affiliation:

1. Department of Pharmaceutical Sciences, School of Pharmacy, Texas Tech University Health Sciences Center, Amarillo, Texas 79106, United States

2. Department of Pharmaceutical Sciences, University of Nebraska Medical Center, Omaha, Nebraska 68198, United States

3. UNMC Center for Drug Discovery, University of Nebraska Medical Center, Omaha, Nebraska 68198, United States

Funder

National Center for Advancing Translational Sciences

Texas Tech University

University of Nebraska Medical Center

Publisher

American Chemical Society (ACS)

Subject

Pharmacology (medical),Pharmacology

Link

https://pubs.acs.org/doi/pdf/10.1021/acsptsci.0c00077

Reference84 articles.

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