Nedosiran, a Candidate siRNA Drug for the Treatment of Primary Hyperoxaluria: Design, Development, and Clinical Studies-Reference-Cited by-同舟云学术

Nedosiran, a Candidate siRNA Drug for the Treatment of Primary Hyperoxaluria: Design, Development, and Clinical Studies

Published:2022-09-21 Issue:11 Volume:5 Page:1007-1016
ISSN:2575-9108
Container-title:ACS Pharmacology & Translational Science
language:en
Short-container-title:ACS Pharmacol. Transl. Sci.

Author:

Liu Anna¹,Zhao Jenny¹,Shah Milan¹,Migliorati Julia M.¹,Tawfik Sherouk M.¹,Bahal Raman¹^ORCID,Rasmussen Theodore P.¹,Manautou Jose E.¹,Zhong Xiao-bo¹^ORCID

Affiliation:

1. Department of Pharmaceutical Sciences, School of Pharmacy, University of Connecticut, Storrs, Connecticut06269, United States

Funder

National Institute of General Medical Sciences

Publisher

American Chemical Society (ACS)

Subject

Pharmacology (medical),Pharmacology

Link

https://pubs.acs.org/doi/pdf/10.1021/acsptsci.2c00110

Reference45 articles.

1. Primary hyperoxaluria type 1 in The Netherlands: prevalence and outcome

2. Changing pattern of primary hyperoxaluria in Switzerland

3. Epidemiology of primary hyperoxaluria type 1

4. SP771HISTORY OF RENAL AND OCULAR FINDINGS IN PRIMARY HYPEROXALURIA: FROM OXALIS ACETOSELLA TO THE MULBERRY CALCULUS, CKD, RETINOPATHY AND SYSTEMIC OXALOSIS

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