Evaluation of Chemically Modified Nucleic Acid Analogues for Splice Switching Application

Author:

Le Bao T.123ORCID,Chen Suxiang12,Veedu Rakesh N.123ORCID

Affiliation:

1. Centre for Molecular Medicine and Innovative Therapeutics, Health Futures Institute, Murdoch University, Murdoch, Western Australia 6150, Australia

2. Precision Nucleic Acid Therapeutics, Perron Institute for Neurological and Translational Science, Nedlands, Western Australia 6009, Australia

3. ProGenis Pharmaceuticals Pty Ltd., Bentley, Western Australia 6102, Australia

Funder

Perron Institute for Neurological and Translational Science

McCusker Charitable Foundation

Caruthers Family Foundation

ProGenis Pharmaceuticals Pty Ltd

Publisher

American Chemical Society (ACS)

Subject

General Chemical Engineering,General Chemistry

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