Enzyme replacement and beyond
Author:
Affiliation:
1. ; Department of Human Genetics; Mount Sinai School of Medicine of New York University, New York; NY 10029 USA
Publisher
Wiley
Subject
Genetics(clinical),Genetics
Link
http://onlinelibrary.wiley.com/wol1/doi/10.1023/A:1010331404448/fullpdf
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3. Gaucher's disease: studies of gene transfer to haematopoietic cells;Barranger;Baillières Clin Haematol,1997
4. Therapeutic response to intravenous infusions of glucocerebrosidase in a patient with Gaucher disease;Barton;Proc Natl Acad Sci USA,1990
5. Replacement therapy for inherited enzyme deficiency-macrophage-targeted glucocerebrosidase for Gaucher's disease;Barton;N Engl J Med,1991
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