Murine mucopolysaccharidosis type VII: The impact of therapies on the clinical course and pathology in a murine model of lysosomal storage disease-Reference-Cited by-同舟云学术

Murine mucopolysaccharidosis type VII: The impact of therapies on the clinical course and pathology in a murine model of lysosomal storage disease

Published:1998-08 Issue:5 Volume:21 Page:575-586
ISSN:0141-8955
Container-title:Journal of Inherited Metabolic Disease
language:en
Short-container-title:J Inherit Metab Dis

Author:

Vogler C.¹,Sands M. S.²,Galvin N.¹,Levy B.¹,Thorpe C.¹,Barker J.³,Sly W. S.⁴

Affiliation:

1. ; Department of Pathology; Saint Louis University School of Medicine; St. Louis Missouri USA

2. ; Division of Bone Marrow Transplantation and Stem Cell Biology, Department of Internal Medicine and Genetics; Washington University School of Medicine; St Louis Missouri USA

3. The Jackson Laboratory; Bar Harbor; Maine USA

4. ; Edward A. Doisy Department of Biochemistry and Molecular Biology; Saint Louis University School of Medicine; St. Louis Missouri USA

Publisher

Wiley

Subject

Genetics (clinical),Genetics

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1023/A:1005423222927/fullpdf

Reference41 articles.

1. Behavioral consequences of bone marrow transplantation in the treatment of murine mucopolysac-charidosis type VII;Bastedo;J Clin Invest,1994

2. Pathology of the ear in murine mucopolysaccharidosis type VII;Berry;L ab Invest,1994

3. Enzyme replacement therapy for Gaucher's disease;Beutler;Blood,1991

4. Murine mucopolysaccharidosis type VII; characterization of a mouse with βglucuronidase deficiency;Birkenmeier;J Clin Invest,1989

5. Increased life span and correction of metabolic defects in murine mucopolysaccharidosis type VII after syngeneic bone marrow transplantation;Birkenmeier;Blood,1991

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