Gene Therapy for Monogenic Inherited Disorders: Opportunities and Challenges-Reference-Cited by-同舟云学术

Gene Therapy for Monogenic Inherited Disorders: Opportunities and Challenges

Published:2020-12-21 Issue: Volume: Page:
ISSN:1866-0452
Container-title:Deutsches Ärzteblatt international
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Author:

Kirschner Janbernd,Cathomen Toni

Publisher

Deutscher Arzte-Verlag GmbH

Subject

General Medicine

Reference40 articles.

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5. Pasi KJ, Rangarajan S, Mitchell N, et al.: Multiyear follow-up of AAV5-hFVIII-SQ gene therapy for hemophilia A. N Engl J Med 2020; 382: 29–40

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