The efficacy and safety of romiplostim in the treatment of thrombocytopenia in pediatric patients with Wiskott–Aldrich syndrome: the results of a retrospective study-Reference-Cited by-同舟云学术

The efficacy and safety of romiplostim in the treatment of thrombocytopenia in pediatric patients with Wiskott–Aldrich syndrome: the results of a retrospective study

Published:2021-01-11 Issue:4 Volume:19 Page:39-49
ISSN:2414-9314
Container-title:Pediatric Hematology/Oncology and Immunopathology
language:
Short-container-title:Voprosy gematologii/onkologii i immunopatologii v pediatrii

Author:

Khoreva A. L.¹^ORCID,Abramova I. N.¹^ORCID,Deripapa E. V.¹^ORCID,Rodina Yu. A.¹^ORCID,Roppelt A. A.¹^ORCID,Burlakov V. I.¹^ORCID,Pershin D. E.¹^ORCID,Larin S. S.¹^ORCID,Raykina E. V.¹^ORCID,Varlamova T. V.¹,Kieva A. M.¹^ORCID,Voronin K. A.¹^ORCID,Maschan A. A.¹^ORCID,Novichkova G. A.¹^ORCID,Shcherbina A. Yu.¹^ORCID

Affiliation:

1. Dmitry Rogachev National Medical Research Center of Pediatric Hematology, Oncology and Immunology of Ministry of Healthcare of the Russian Federation

Publisher

Fund Doctors, Innovations, Science for Children

Subject

Oncology,Hematology,Immunology,Immunology and Allergy,Pediatrics, Perinatology, and Child Health

Reference39 articles.

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2. Moratto D., Giliani S., Bonfim C., Mazzolari E., Fischer A., Ochs H.D., et al. Long-term outcome and lineage-specific chimerism in 194 patients with WiskottAldrich syndrome treated by hematopoietic cell transplantation in the period 1980-2009: an international collaborative study. Blood 2011; 118: 1675–84. DOI: 10.1182/blood-2010-11-319376

3. Balashov D., Laberko A., Shcherbina A., Trakhtman P., Abramov D., Gutovskaya E., et al. Conditioning Regimen with Plerixafor Is Safe and Improves the Outcome of TCRab+ and CD19+ Cell-Depleted Stem Cell Transplantation in Patients with Wiskott–Aldrich Syndrome. Biol Blood Marrow Transplant 2018; 24 (7): 1432–40. DOI: 10.1016/j.bbmt.2018.03.006

4. Ferrua F., Marangoni F., Aiuti A., Roncarolo M.G. Gene therapy for WiskottAldrich syndrome: History, new vectors, future directions. J Allergy Clin Immunol 2020; 146 (2): 262–5. DOI: 10.1016/j.jaci.2020.06.018

5. Rivers E., Worth A., Thrasher A.J., Burns S.O. Bleeding and splenectomy in Wiskott–Aldrich syndrome: A single-centre experience. J Allergy Clin Immunol Pract 2019; 7: 1042–4. DOI: 10.1016/j.jaip.2018.07.009