Weekly Cyclodextrin Administration Normalizes Cholesterol Metabolism in Nearly Every Organ of the Niemann-Pick Type C1 Mouse and Markedly Prolongs Life-Reference-Cited by-同舟云学术

Weekly Cyclodextrin Administration Normalizes Cholesterol Metabolism in Nearly Every Organ of the Niemann-Pick Type C1 Mouse and Markedly Prolongs Life

Published:2010-10 Issue:4 Volume:68 Page:309-315
ISSN:0031-3998
Container-title:Pediatric Research
language:
Short-container-title:Pediatr Res

Author:

Ramirez Charina M,Liu Benny,Taylor Anna M,Repa Joyce J,Burns Dennis K,Weinberg Arthur G,Turley Stephen D,Dietschy John M

Publisher

Springer Science and Business Media LLC

Subject

Pediatrics, Perinatology and Child Health

Reference19 articles.

1. Murine Model of Niemann-Pick C Disease: Mutation in a Cholesterol Homeostasis Gene

2. Receptor-mediated and bulk-phase endocytosis cause macrophage and cholesterol accumulation in Niemann-Pick C disease

3. Molecular, Anatomical, and Biochemical Events Associated with Neurodegeneration in Mice with Niemann-Pick Type C Disease

4. Cholesterol Accumulation in NPC1-Deficient Neurons Is Ganglioside Dependent

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