Efficacy and Safety of Taliglucerase Alfa for the Treatment of Gaucher Disease: A 9-Year Experience-Reference-Cited by-同舟云学术

Efficacy and Safety of Taliglucerase Alfa for the Treatment of Gaucher Disease: A 9-Year Experience

Published:2022 Issue: Volume:10 Page:
ISSN:2326-4594
Container-title:Journal of Inborn Errors of Metabolism and Screening
language:
Short-container-title:J. inborn errors metab. screen.

Author:

Paskulin Livia d’Avila¹^ORCID,Starosta Rodrigo Tzovenos²^ORCID,Vairo Filippo Pinto e³^ORCID,Krug Bárbara C.⁴,Picon Paulo⁵,Schwartz Ida Vanessa Doederlein⁶^ORCID

Affiliation:

1. Universidade Federal do Rio Grande do Sul, Brazil; Universidade Federal do Rio Grande do Sul, Brazil

2. Universidade Federal do Rio Grande do Sul, Brazil; Washington University in Saint Louis, USA

3. Mayo Clinic, USA; Mayo Clinic, USA

4. Hospital de Clínicas de Porto Alegre, Brazil

5. Hospital de Clínicas de Porto Alegre, Brazil; Universidade Federal do Rio Grande do Sul, Brazil

6. Universidade Federal do Rio Grande do Sul, Brazil; Universidade Federal do Rio Grande do Sul, Brazil; Hospital de Clínicas de Porto Alegre, Brazil

Publisher

FapUNIFESP (SciELO)

Subject

Genetics (clinical),Endocrinology, Diabetes and Metabolism,Pediatrics, Perinatology and Child Health

Link

http://www.scielo.br/scielo.php?script=sci_pdf&pid=S2326-45942022000100303&tlng=en

Reference30 articles.

1. Phenotype, diagnosis, and treatment of Gaucher’s disease;Grabowski GA;Lancet,2008

2. Gaucher cells demonstrate a distinct macrophage phenotype and resemble alternatively activated macrophages;Boven LA;Am J Clin Pathol,2004

3. Replacement therapy for inherited enzyme deficiency--macrophage-targeted glucocerebrosidase for Gaucher's disease;Barton NW;N Engl J Med,1991

4. Replacement therapy with imiglucerase for type 1 Gaucher's disease;Zimran A;Lancet,1995

5. Enzyme therapy in type 1 Gaucher disease: comparative efficacy of mannose- terminated glucocerebrosidase from natural and recombinant sources;Grabowski GA;Ann Intern Med,1995

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1. Taliglucerase alfa in the longterm treatment of children and adolescents with type 1 Gaucher disease: the Albanian experience;Frontiers in Pediatrics;2024-02-23

2. Multiple drugs;Reactions Weekly;2023-07-01