Author:
Cox Timothy M.,Tylki-Szymańska Anna,Aymé Ségolène,Dooms Marc
Subject
Pharmacology (medical),Pharmacology
Reference9 articles.
1. We are a nonprofit fighting poverty, disease and inequity around the world2022
2. The road to biosimilars in rare diseases - ongoing lessons from Gaucher disease;Drelichman;Am. J. Hematol.,2020
3. Legal framework: Orphan designation2000
4. Improved Diagnosis of rare disease patients through systematic detection of runs of homozygosity.;Matalonga;J. Mol. Diagn.,2020