1. Horae Gene Therapy Center, UMass Chan Medical School, Worcester, MA 01605, USA
2. Spirovant Sciences, Inc., Philadelphia, PA 19104, USA
3. Department of Microbiology and Physiological Systems, UMass Chan Medical School, Worcester, MA 01605, USA
4. Li Weibo Institute of Rare Diseases Research, UMass Chan Medical School, Worcester, MA 01605, USA