Use of an adeno‐associated virus serotype Anc80 to provide durable cure of phenylketonuria in a mouse model-Reference-Cited by-同舟云学术

Use of an adeno‐associated virus serotype Anc80 to provide durable cure of phenylketonuria in a mouse model

Published:2021-08-19 Issue:6 Volume:44 Page:1369-1381
ISSN:0141-8955
Container-title:Journal of Inherited Metabolic Disease
language:en
Short-container-title:Jrnl of Inher Metab Disea

Author:

Kaiser Robert A.¹²^ORCID,Weber Nicholas D.³,Trigueros‐Motos Laia³,Allen Kari L.²,Martinez Michael⁴,Cao William²,VanLith Caitlin J.²,Hillin Lori G.²,Douar Anne⁵,González‐Aseguinolaza Gloria³⁶⁷^ORCID,Aldabe Rafael⁶,Lillegard Joseph B.¹²⁸

Affiliation:

1. Children's Hospitals and Clinics of Minnesota Minneapolis Minnesota USA

2. Department of Surgery Mayo Clinic Rochester Minnesota USA

3. Vivet Therapeutics S.L. Pamplona Spain

4. Department of Molecular and Medical Genetics Oregon Health & Science University Portland Oregon USA

5. Vivet Therapeutics S.A.S. Paris France

6. Division of Gene Therapy and Regulation of Gene Expression CIMA Universidad de Navarra Pamplona Spain

7. Instituto de Investigación Sanitaria de Navarra (IdISNA) Pamplona Spain

8. Pediatric Surgical Associates Minneapolis Minnesota USA

Publisher

Wiley

Subject