1. University of Pittsburgh Pittsburgh Pennsylvania USA
2. Ann & Robert H. Lurie Children's Hospital Chicago Illinois USA
3. Boston Children's Hospital Boston Massachusetts USA
4. University of Utah Salt Lake City Utah USA
5. Vanderbilt University Medical Center Nashville Tennessee USA
6. USF Health Morsani College of Medicine Tampa Florida USA
7. Children's National Health System Washington District of Columbia USA
8. Great Ormond Street Hospital and Institute of Child Health NIHR Biomedical Research Center (BRC), UCL London UK
9. National Hospital for Neurology and Neurosurgery London UK
10. Ultragenyx Pharmaceutical Inc. Novato California USA