Phase II trial of pirfenidone in children and young adults with neurofibromatosis type 1 and progressive plexiform neurofibromas

Author:

Widemann Brigitte C.1,Babovic-Vuksanovic Dusica2,Dombi Eva1,Wolters Pamela L.1,Goldman Stewart3,Martin Staci1,Goodwin Anne1,Goodspeed Wendy1,Kieran Mark W.4,Cohen Bruce5,Blaney Susan M.6,King Allison7,Solomon Jeffrey8,Patronas Nicholas9,Balis Frank M.110,Fox Elizabeth110,Steinberg Seth M.11,Packer Roger J12

Affiliation:

1. Pediatric Oncology Branch; National Cancer Institute; Bethesda Maryland

2. Department of Medical Genetics; Mayo College of Medicine; Rochester Minnesota

3. Ann and Robert H Lurie Children's Hospital of Chicago; Chicago Illinois

4. Dana-Farber/Children's Hospital Cancer Center; Boston Massachusetts

5. Cleveland Clinic; Cleveland Ohio

6. Texas Children's Hospital; Houston Texas

7. St. Louis Children's Hospital; St. Louis Missouri

8. Expert Image Analysis LLC; Potomac Maryland

9. Diagnostic Radiology Department, Clinical Center; National Institutes of Health; Bethesda Maryland

10. The Children's Hospital of Philadelphia; Philadelphia Pennsylvania

11. Biostatistics and Data Management Section; National Cancer Institute; Bethesda Maryland

12. Children's National Medical Center; Washington District of Columbia

Funder

Department of Defense

FDA Orphan Fund Program Grant

Publisher

Wiley

Subject

Oncology,Hematology,Pediatrics, Perinatology, and Child Health

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