Efficacy of systemic sirolimus in the treatment of generalized lymphatic anomaly and Gorham

Efficacy of systemic sirolimus in the treatment of generalized lymphatic anomaly and Gorham–Stout disease

Published:2019-01-22 Issue:5 Volume:66 Page:e27614
ISSN:1545-5009
Container-title:Pediatric Blood & Cancer
language:en
Short-container-title:Pediatr Blood Cancer

Author:

Ricci Kiersten W.¹^ORCID,Hammill Adrienne M.¹,Mobberley‐Schuman Paula¹,Nelson Stephen C.²^ORCID,Blatt Julie³^ORCID,Bender Julia L. Glade⁴,McCuaig Catherine C.⁵,Synakiewicz Anna⁶^ORCID,Frieden Ilona J.⁷,Adams Denise M.⁸^ORCID

Affiliation:

1. Hemangioma and Vascular Malformation CenterDivision of HematologyCancer and Blood Diseases InstituteCincinnati Children's Hospital Medical CenterUniversity of Cincinnati College of Medicine Cincinnati Ohio

2. Department of Pediatric Hematology and OncologyChildren's Minnesota Hematology Oncology Minneapolis Minnesota

3. Division of Pediatric Hematology OncologyUniversity of North Carolina Chapel Hill North Carolina

4. Division of Pediatric HematologyOncologyand Stem Cell TransplantationColumbia University Medical Center New York City New York

5. Sainte‐Justine University Hospital Center Montreal Canada

6. Department of PediatricsHematology and OncologyMedical University of Gdańsk Gdańsk Poland

7. Department of DermatologyUniversity of California San Francisco San Francisco California

8. Vascular Anomalies CenterDivision of Hematology/OncologyCancer and Blood Disorders CenterBoston Children's Hospital Boston Massachusetts

Funder

U.S. Food and Drug Administration

National Center for Advancing Translational Sciences

Publisher

Wiley

Subject

Oncology,Hematology,Pediatrics, Perinatology, and Child Health

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/pbc.27614

Reference30 articles.

1. Gorham-Stout disease and generalized lymphatic anomaly—clinical, radiologic, and histologic differentiation

2. AitroM BroeckerK O'HareMJ et al.An observational study of long‐term outcomes in complicated lymphatic anomalies: The Lymphatic Anomalies Registry. Abstract presented at: Biannual Meeting of International Society for the Study of Vascular Anomalies; April 27–28 2016; Buenos Aires Argentina.

3. Medical Therapy for Pediatric Vascular Anomalies

4. Lymphangiogenic factors, mechanisms, and applications

5. Genetics of lymphatic anomalies

Cited by 90 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. PIK3CA-Related Disorders: From Disease Mechanism to Evidence-Based Treatments;Annual Review of Genomics and Human Genetics;2024-08-27

2. Pediatric cerebrospinal fluid rhinorrhea caused by low flow vascular anomaly of the temporal bone: A case series;International Journal of Pediatric Otorhinolaryngology;2024-07

3. Preventative treatment of tuberous sclerosis complex with sirolimus: Phase I safety and efficacy results;Annals of the Child Neurology Society;2024-04-22

4. Psychometric Evaluation of the “Providing Validation” Measure in Vascular Anomalies;Journal of Vascular Anomalies;2024-04-02

5. Disorders of the Lymphatic System;Rook's Textbook of Dermatology;2024-03-19