Gene therapy for Whiskott–Aldrich syndrome: The latest news-Reference-Cited by-同舟云学术

Gene therapy for Whiskott–Aldrich syndrome: The latest news

Published:2022-04 Issue:4 Volume:12 Page:
ISSN:2001-1326
Container-title:Clinical and Translational Medicine
language:en
Short-container-title:Clinical & Translational Med

Author:

Cavazzana Marina¹²³,Thrasher Adrian⁴

Affiliation:

1. Department of Biotherapy Hôpital Universitaire Necker‐Enfants Malades Groupe Hospitalier Paris Centre Assistance Publique–Hopitaux de Paris Paris France

2. Biotherapy Clinical Investigation Center Groupe Hospitalier Universitaire Paris Centre Assistance Publique‐Hôpitaux de Paris Paris France

3. Imagine Institute Université Paris Paris France

4. Molecular and Cellular Immunology Section UCL Great Ormond Street Institute of Child Health University College London London UK

Publisher

Wiley

Subject

Molecular Medicine,Medicine (miscellaneous)

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1002/ctm2.815

Reference19 articles.

1. The Wiskott-Aldrich syndrome in the United States and Canada (1892–1979)

2. Lessons from the Wiskott–Aldrich Syndrome

3. [Mutation analysis of WASP gene and prenatal diagnosis of Wiskott‐Aldrich syndrome];Liu N;Zhonghua Er Ke Za Zhi,2014

4. Clinical course of patients with WASP gene mutations

5. Mutations of the Wiskott-Aldrich Syndrome Protein (WASP): hotspots, effect on transcription, and translation and phenotype/genotype correlation

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1. Haploidentical bone marrow transplantation in a pediatric patient with Wiskott-Aldrich syndrome. A case report;Archivos Argentinos de Pediatria;2024-02-01

2. Recent advances in hematopoietic gene therapy for genetic disorders;Archives de Pédiatrie;2023-11

3. Tailored treatments in inborn errors of immunity associated with atopy (IEIs-A) with skin involvement;Frontiers in Pediatrics;2023-03-22