Systemic human minidystrophin gene transfer improves functions and life span of dystrophin and dystrophin/utrophin-deficient mice
Author:
Funder
National Institutes of Health
Muscular Dystrophy Association
Publisher
Wiley
Subject
Orthopedics and Sports Medicine
Link
http://onlinelibrary.wiley.com/wol1/doi/10.1002/jor.20781/fullpdf
Reference28 articles.
1. Dystrophin: the protein product of the Duchenne muscular dystrophy locus;Hoffman;Cell,1987
2. Gene therapy of muscular dystrophy;Chamberlain;Hum Mol Genet,2002
3. Viral-mediated gene therapy for the muscular dystrophies: successes, limitations and recent advances;Odom;Biochim Biophys Acta,2007
4. Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model;Wang;Proc Natl Acad Sci USA,2000
5. Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy;Harper;Nat Med,2002
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