A Potent Inhibitor of Protein Sequestration by Expanded Triplet (CUG) Repeats that Shows Phenotypic Improvements in aDrosophilaModel of Myotonic Dystrophy-Reference-Cited by-同舟云学术

A Potent Inhibitor of Protein Sequestration by Expanded Triplet (CUG) Repeats that Shows Phenotypic Improvements in aDrosophilaModel of Myotonic Dystrophy

Published:2016-06-01 Issue:13 Volume:11 Page:1428-1435
ISSN:1860-7179
Container-title:ChemMedChem
language:en
Short-container-title:ChemMedChem

Author:

Luu Long M.¹,Nguyen Lien¹,Peng Shaohong²,Lee JuYeon¹,Lee Hyang Yeon¹,Wong Chun-Ho¹,Hergenrother Paul J.¹,Chan H. Y. Edwin²,Zimmerman Steven C.¹^ORCID

Affiliation:

1. Department of Chemistry; University of Illinois at Urbana-Champaign; 600 S. Mathews Ave. Urbana IL 61801 USA

2. Laboratory of Drosophila Research and School of Life Sciences; The Chinese University of Hong Kong; Shatin, N.T. Hong Kong SAR P.R. China

Funder

National Institutes of Health

Muscular Dystrophy Association

Lui Che Woo Institute of Innovative Medicine BRAIN Initiative

Publisher

Wiley

Subject

Organic Chemistry,General Pharmacology, Toxicology and Pharmaceutics,Molecular Medicine,Drug Discovery,Biochemistry,Pharmacology

Reference49 articles.

1. Therapeutics development in myotonic dystrophy type 1

2. Perspectives on gene therapy in myotonic dystrophy type 1

3. Myotonic Dystrophy Mutation: an Unstable CTG Repeat in the 3′ Untranslated region of the Gene

4. Myotonic dystrophy: Emerging mechanisms for DM1 and DM2

5. Pathogenic mechanisms of myotonic dystrophy

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